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Pompe Disease in the US Market- Trends, Drivers, Strategies, Applications and Competitive Landscape 2019

Monday, October 24, 2016 3:22
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The Pompe Disease in the US Industry report covers the present scenario and the growth prospects of the Pompe Disease in the US Market for 2016-2019. Pompe Disease in the US Market report focuses on the major drivers and restraints for the key players. To calculate the market size, the report considers both the direct revenue and the indirect revenue of the vendors.

Pompe disease, a type of LSD, is caused by mutations in the GAA gene. These mutations inhibit the mechanism of action of GAA, an enzyme responsible for catabolizing glycogen, resulting in accumulation of glycogen in the lysosomes of the cells. The buildup of glycogen in certain organs and tissues, especially in the muscles, hinders the normal functions of the organs. Pompe disease can be further classified as infantile-onset and adult-onset Pompe disease. As the disease is an autosomal recessive hereditary disorder, both parents are carriers and can pass one copy of the mutated gene to their offspring. The disease affects both men and women.

Pompe disease market in the US to grow at a CAGR of 10.68 % over the period 2014-2019.

Browse more detail information about Pompe Disease in the US Market Report at:

The report covers the market landscape and its growth prospects over the coming years. The report also includes a discussion of the key vendors operating in this market.

Key Vendors in Pompe Disease in the US Market

• Amicus Therapeutics

• BioMarin Pharmaceutical

• Genzyme

Other prominent vendors

• Audentes Therapeutics

• EpiVax

• Oxyrane

• Sangamo BioSciences

• Valerion Therapeutics

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The Pompe Disease in the US Market is divided into the following segments based on geography:

• Americas



Pompe Disease in the US Market Opportunities During 2016-2019:

With a purpose of enlightening new entrants about the possibilities in this market, this report investigates new project feasibility. Various details about the manufacturing process such as market drivers, impact of drivers, market challenges and impact of drivers and challenges, market trends, vendor landscape analysis and so on, is discussed in the report

Pompe Disease in the US Market Dynamics:

Market driver:

• Special provision for orphan drugs

Market challenge:

• Limited patient population

Market trend:

• Growing public awareness

In the end, the report makes some important proposals for a new project of Pompe Disease in the US Industry before evaluating its feasibility. Overall, the report provides an in-depth insight of Global Pompe Disease in the US Market 2016-2019 industry covering all important parameters.

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Key questions answered in this Pompe Disease in the US Market 2016-2019 report

• What will the market size be in 2019 and what will the growth rate be?

• What are the key market trends?

• What is driving this market?

• What are the challenges to market growth?

• Who are the key vendors in this market space?

• What are the market opportunities and threats faced by the key vendors?

• What are the strengths and weaknesses of the key vendors?

Get Discount on Pompe Disease in the US Market Research Report at:

List of Exhibits

Exhibit 01: Product offerings

Exhibit 02: Pompe disease market in US 2014-2019 ($ millions)

Exhibit 03: Drivers and challenges for Pompe disease market in US

Exhibit 04: Five forces analysis

Exhibit 05: Snapshot of Pompe disease

Exhibit 06: Classification of Pompe disease

Exhibit 07: Signs and symptoms of Pompe disease

Exhibit 08: Differential diagnosis for Pompe disease in infants

Exhibit 09: Differential diagnosis for Pompe disease in children and adults

Exhibit 10: Biochemical pathway of Pompe disease

Exhibit 11: Approaches to treat Pompe disease

Exhibit 12: Economic burden: Pompe disease

Exhibit 13: Orphan drug development and regulatory challenges

Exhibit 14: Pipeline portfolio of Pompe disease market in US


About Absolute Report:

Absolute Reports is an upscale platform to help key personnel in the business world in strategizing and taking visionary decisions based on facts and figures derived from in-depth market research. We are one of the top report resellers in the market dedicated towards bringing you an ingenious concoction of data parameters.


Mr. Ameya Pingaley

Absolute Reports

+1-408 520 9750


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